42:12

Tips & Tricks on Insurance and ABA Therapy

12:04

ADVANCE 2024: Introduction keynote

01:48:05

ADVANCE 2024: Deep Dive Gene Therapy Considerations

01:10:51

ADVANCE 2024: Impact of Sanfilippo on the Retina

01:18:49

ADVANCE 2024: Deep Dive: Supporting Health Through Nutrition

30:10

ADVANCE 2024: The Advantage of Qualitative Interviews in Clinical Trials

43:53

ADVANCE 2024: Updates on Clinical Trials for Sanfilippo Syndrome (Part 1)

28:49

ADVANCE 2024: Cure Sanfilippo Foundation Programs Affecting Change

59:48

ADVANCE 2024: Advances in Preclinical Research For Sanfilippo

29:38

ADVANCE 2024: Sanfilippo In My Voice: Experience with Brain & Tissue Donation

01:06:23

ADVANCE 2024: Deep Dive: Mitochondria & Metabolism in Sanfilippo

01:04:31

ADVANCE 2024: Drug Repurposing Studies for Sanfilippo Syndrome

24:20

ADVANCE 2024: Evidence-Based Architectural Design Strategies for Enriching Environments

30:58

ADVANCE 2024: How does the “Accelerated Approval” process work?

52:09

ADVANCE 2024: Updates on Clinical Trials for Sanfilippo Syndrome (Part 2)

01:59

ADVANCE 2024: Closing from Cure Sanfilippo founders

24:11

ADVANCE 2024: Sanfilippo in My Voice: Our Experience Living with Attenuated Sanfilippo Type B

06:19

ADVANCE 2024: In Memoriam Tribute

09:23

ADVANCE 2024: "How We Do It" families #1 & #2

10:10

ADVANCE 2024: "How We Do It" families #3 & #4

04:51

ADVANCE 2024: "How We Do It" family #5

06:17

ADVANCE 2024: "How We Do It" family #6

11:59

ADVANCE 2024: "How We Do It' family #7

05:34

ADVANCE 2024: "How We Do It" family #8

10:33

ADVANCE 2024: Closing Remarks at the Regan-Udall Meeting with the FDA

03:15

We need a miracle. Save Lydia.

10:51

Cara O'Neill | Qualifying Biomarkers to Support Rare Disease Regulatory Pathways | Closing Speech

31:32

Life with "Attenuated" Sanfilippo Syndrome | The Kohlmorgan Family

53:33

Durable Medical Equipment (DME) and Sanfilippo Syndrome

54:51

What is Assistive Technology and how can it help your child communicate?

03:16

First time parents watch video they hope will save their daughter

01:19:38

Update on Ultragenyx's Sanfilippo syndrome Type A Gene Therapy program (UX111) - March 26, 2024

02:58

Saving Veda from Sanfilippo syndrome

03:10

A Message to You on the 10-Year Anniversary of Cure Sanfilippo Foundation

11:07

Development of Global Consensus Clinical Care Guidelines for Sanfilippo Syndrome, WORLDSymposium2023

03:31

Parents' first watch of a video they hope will save their daughter Liv

03:15

This video can save our 3-year-old daughter's life: #SavingLiv

00:15

Saving Liv - Coming Saturday, Dec. 3

08:20

New Sanfilippo drug repurposing clinical trial; updates on other research + more

03:29:34

ADVANCE 22 Sanfilippo Conference - Day 1, Part 1

02:14:32

ADVANCE 22 Sanfilippo conference - Day 2, Part 3

02:05:55

ADVANCE 22 Sanfilippo conference - Day 2, Part 2

02:31:14

ADVANCE 22 Sanfilippo conference - Day 2, Part 1

02:35:41

ADVANCE 22 Sanfilippo conference - Day 1, Part 2

01:58:48

ADVANCE 22 Sanfilippo conference - Day 1, Part 3

01:01

TikTok For A Cure - Kickoff from @Love_Logan07

03:38

Alina's Story - One more miracle?

08:54

WORLD Symposium highlights Anakinra early results; upcoming gene therapy trial; + more

09:39

Kicking off 2022; upcoming key meeting with FDA; recent grants, WORLD conference, & more

10:37

Anakinra Trial update, Collaboration with UNC, other research updates, Help Simon, & more

06:42

How All Stripes can help Sanfilippo syndrome research

03:04

Help Simon fight to live and play basketball

12:49

BIG WEEK! World Sanfilippo Day & viral campaign, Trivia Gala, All Stripes & more

13:10

Sanfilippo & accelerated approval; newly-diagnosed guide; World Sanfilippo Awareness Day & more

01:05

2021 Step Up to Cure Sanfilippo | Wrap-Up Video

11:06

Why a podcast?; Photobiomodulation research; the costs of pioneering research; + more

10:34

Patient Needs & Culture of the Laboratory; Kickoff 2021 StepUp fundraiser; families milestone & more

11:39

Get-to-know your child worksheet for school; Sanfilippo on TikTok; Inclusion + more

12:02

Free Educator Guide; Dopamine & Reducing Autism Behaviors + more

10:00

In Memory of Reagan; New testing created; $1M granted for 5 new projects + more