03:15

We need a miracle. Save Lydia.

10:51

Cara O'Neill | Qualifying Biomarkers to Support Rare Disease Regulatory Pathways | Closing Speech

31:32

Life with "Attenuated" Sanfilippo Syndrome | The Kohlmorgan Family

53:33

Durable Medical Equipment (DME) and Sanfilippo Syndrome

54:51

What is Assistive Technology and how can it help your child communicate?

03:16

First time parents watch video they hope will save their daughter

01:19:38

Update on Ultragenyx's Sanfilippo syndrome Type A Gene Therapy program (UX111) - March 26, 2024

02:58

Saving Veda from Sanfilippo syndrome

03:10

A Message to You on the 10-Year Anniversary of Cure Sanfilippo Foundation

11:07

Development of Global Consensus Clinical Care Guidelines for Sanfilippo Syndrome, WORLDSymposium2023

03:31

Parents' first watch of a video they hope will save their daughter Liv

03:15

This video can save our 3-year-old daughter's life: #SavingLiv

00:15

Saving Liv - Coming Saturday, Dec. 3

08:20

New Sanfilippo drug repurposing clinical trial; updates on other research + more

03:29:34

ADVANCE 22 Sanfilippo Conference - Day 1, Part 1

02:14:32

ADVANCE 22 Sanfilippo conference - Day 2, Part 3

02:05:55

ADVANCE 22 Sanfilippo conference - Day 2, Part 2

02:31:14

ADVANCE 22 Sanfilippo conference - Day 2, Part 1

02:35:41

ADVANCE 22 Sanfilippo conference - Day 1, Part 2

01:58:48

ADVANCE 22 Sanfilippo conference - Day 1, Part 3

01:01

TikTok For A Cure - Kickoff from @Love_Logan07

03:38

Alina's Story - One more miracle?

08:54

WORLD Symposium highlights Anakinra early results; upcoming gene therapy trial; + more

09:39

Kicking off 2022; upcoming key meeting with FDA; recent grants, WORLD conference, & more

10:37

Anakinra Trial update, Collaboration with UNC, other research updates, Help Simon, & more

06:42

How All Stripes can help Sanfilippo syndrome research

03:04

Help Simon fight to live and play basketball

12:49

BIG WEEK! World Sanfilippo Day & viral campaign, Trivia Gala, All Stripes & more

13:10

Sanfilippo & accelerated approval; newly-diagnosed guide; World Sanfilippo Awareness Day & more

01:05

2021 Step Up to Cure Sanfilippo | Wrap-Up Video

11:06

Why a podcast?; Photobiomodulation research; the costs of pioneering research; + more

10:34

Patient Needs & Culture of the Laboratory; Kickoff 2021 StepUp fundraiser; families milestone & more

11:39

Get-to-know your child worksheet for school; Sanfilippo on TikTok; Inclusion + more

12:02

Free Educator Guide; Dopamine & Reducing Autism Behaviors + more

10:00

In Memory of Reagan; New testing created; $1M granted for 5 new projects + more

10:49

Chan Zuckerberg, Sanfilippo biomarkers & FDA; Anakinra trial update; + more

02:23

Kids on a mission to save their best friend’s life

01:01

Save Connor | #shorts

03:48

Parents' first watch of a video they hope will save dying son

02:27

What Is Sanfilippo Syndrome?

09:54

Cure Sanfilippo - World Symposium 2021

05:02

Cure Sanfilippo Gala 2020 - Mission Moments 4

06:49

Cure Sanfilippo Gala 2020 - Mission Moments 3

07:34

Cure Sanfilippo Gala 2020 - Mission Moments 2

05:17

Cure Sanfilippo Gala 2020 - Mission Moments 1

01:36

Cure Sanfilippo Gala 2020 - Surprise Introduction!

02:58

We thought it was Autism. What we found out...unimaginable.

01:34

2020 "Step Up To Cure Sanfilippo" Highlights Video

01:09

Carson's parents have something to say to you

08:21

Sanfilippo Syndrome and the fight to find a cure | Cure Sanfilippo Foundation

16:14

The most important presentation on Sanfilippo Syndrome

50:48

Q&A Coronavirus and Sanfilippo Syndrome: Dr. Heather Lau

04:56

A Saving Eliza Update - November 2019

02:52

Saving Eliza

00:54

7 year old Beckham wants to save his little sister

02:42

A dog's devotion like you've never seen: Henry and Blair

01:21

7 year old girl wants to save her little brother's life

03:03

The Last Chance to Save My Son's Life, from Childhood Alzheimer's. #SavingCarter

00:19

Eliza working on her singing - May 8, 2017

02:09

Disney Employee makes Magic Memory for Sick Girls