11:02

FDA Natural History Presentation

05:52

LGMD Global Advocacy Summit and FDA Patient Engagement Meeting

13:16

LGMD2I/R9 Ribitol Trial Results

01:43

A Vacation in Florida

10:18

Clinical Trial Readiness in LGMD

08:53

Upcoming Gene Therapy Trials for LGMD2B and 2I

04:55

Rare Disease Day 2022

16:37

LGMD and the Heart

09:10

A Magazine About LGMD

09:01

NMD Role models

01:17

Hope everyone's 2022 is off to a good start!

02:58

Channel Introduction 2022

12:07

When Will There Be an Approved Treatment for Limb Girdle Muscular Dystrophy?

13:07

In Memory of my Caregiver

12:24

The Large Mouse, Hamlet Antibody, Western Blots (and Geek Humor!)

20:32

2021 Gene Therapy Update part 2

14:48

LGMD Gene Therapy 2021 Update

15:50

A Non-Gene Therapy Clinical Trial for (One Subtype of) LGMD.

17:36

Lemonade Recipes: My story of living with LGMD and my journey into advocacy.

07:50

What's been happening with me this year?

03:57

Thanks!

09:47

FDA Patient Listening Session on LGMDs

01:13

Quick channel update

06:50

Patient Listening Session on Limb Girdle Muscular Dystrophies

15:27

Gene Editing Part 2

05:49

Exciting News From a Friend

17:09

Bad News From a Gene Therapy Trial

11:19

Gene Editing Part 1

06:41

Should We Rename Penny Lane??

12:35

Gene Transfer Therapy: Approach and Limitations

09:56

LGMD2E gene therapy update: expression results for higher dosage

13:24

Genetics, Race, and Healthcare Access

12:06

Muscle Stem Cell Therapy: Potential and Issues

08:59

Muscle structure, growth, regeneration, and stem cells

13:40

Quarantine with the Beatles part 2

12:00

Neuromuscular Gene Therapy Update April 2020

13:51

Quarantine with the Beatles! part 1

08:41

Social distancing, equitable care for people with disabilities, and mental well being at home

08:21

COVID-19 update March 15

11:29

COVID-19 update from Seattle March 8 2020

10:06

COVID-19 in my area

11:07

Leap Day, Rare Disease Day, and LGMD gene therapy update

14:39

Clinical Trials as Applied to Testing Gene Therapies Part 2: Outcome Measures and Power Calculations

02:10

Thanksgiving

16:16

Clinical Trials of Gene Therapy Part 1: Placebo or Not?

09:31

My Reluctant Journey into Advocacy

03:17

Thank you, viewers! And some video links!

08:35

Gene therapy results for Limb Girdle Muscular Dystrophy—Wow!

11:22

Nomenclature of LGMDs

06:16

Limb Girdle Muscular Dystrophy Awareness Day 2019

07:51

Worrying, a.k.a. Anticipatory Anxiety. (You don’t need to!)

05:24

Friendships: Online vs. In Person

08:25

2019 National LGMD Conference!

01:30

A Fun Video Chat!

14:09

Introduction to Genetics Part 2 of 3

10:17

Introduction to Genetics Part 1 of 3

08:56

Development of gene therapies for LGMDs and other NMDs: where things stand in 2019

11:14

Preview of the National Limb Girdle Muscular Dystrophy Conference

03:11

Bright Colors, and Stretching Myself by Organizing a Conference

07:02

Relationships and Disability